Gene-editing Therapy NTLA-2001 Given Orphan Drug Status by FDA
fapnewstoday.com The U.S. Food and Drug Administration (FDA) has given orphan drug designation to NTLA- 2001, an investigational gene-editing therapy for familial amyloid polyneuropathy (FAP) and other forms of transthyretin (ATTR) amyloidosis. … The aim of NTLA-2001 is to disrupt the TTR gene, thus decreasing transthyretin production and preventing the buildup of these harmful protein […]
CRISPR-Cas9 In Vivo Gene Editing for Transthyretin Amyloidosis
Julian D. Gillmore et al. Transthyretin amyloidosis, also called ATTR amyloidosis, is a life-threatening disease characterized by progressive accumulation of misfolded transthyretin (TTR) protein in tissues, predominantly the nerves and heart. NTLA-2001 is an in vivo gene-editing therapeutic agent that is designed to treat ATTR amyloidosis by reducing the concentration of TTR in serum. It […]
Food Freedom – Part 1: The Genetic Engineering and Synthesization of Our Food System
Lucy Crisetig With Covid policies reshaping everything from farmland ownership to meat processing to restaurant eating to food costs and availability, it’s clear that critical battle lines are being redrawn. One of the most disturbing new battlefronts has to do with the most age-old of rights, the right to grow, raise, harvest, produce and consume […]
Emerging Techniques in Biotechnology Pose New Risks to the Non-GMO Supply Chain
Non-GMO Project Is it possible to create a non-GMO product using genetic engineering? While that might seem ludicrous to most of us, biotechnology companies have mounted an aggressive campaign to convince the world that the products of new genetic engineering techniques such as CRISPR are, in fact, non-GMO. Although this is completely unsupported by the […]
Synthetic Biology Test Could Force the Natural Products Industry to Define Its Position
Melaina Juntti Meatless Impossible Burgers that “bleed” just like the real deal. Creamy dairy-free ice cream made with Perfect Day’s nonanimal whey protein. Dietary supplements containing “nature-identical” astaxanthin, resveratrol or collagen made from fermented yeast, bacteria or other microorganisms. These and many other tech-spawned products have flooded the market in recent years, even penetrating the natural […]
